Exon Skipping and Inclusion Therapies

Methods and Protocols

569 Seiten, Taschenbuch

Kurzbeschreibung des Verlags

This book presents a comprehensive collection of detailed state-of-the-art exon skipping and splices modulation protocols. Chapters detail 14 genetic diseases, AON-mediated therapies, and CRISPR/Cas9-mediated gene editing therapies. Written in the highly successful Methods in Molecular Biology series format, chapters include introductions to their respective topics, lists of the necessary materials and reagents, step-by-step, readily reproducible laboratory protocols, and tips on troubleshooting and avoiding known pitfalls.

Authoritative and cutting-edge, Exon Skipping and Inclusion Therapies: Methods and Protocols aims to help researchers initiate the development of next-generation therapies.

• Reihe: Methods in Molecular Biology
• Themen: Medizin Vorklinische Medizin, Grundlagenwissenschaften Genetik, Medizin
• ISBN: 9781493993543
• Sprache: Englisch
• Erscheinungsdatum: 10.12.2019
• Größe: 25.4 x 17.8 cm
• Verlag: Springer US
• Herausgegeben von: Toshifumi Yokota, Rika Maruyama